Duchenne muscular dystrophy
FDA Approves Duvyzat for DMD
The FDA approved Duvyzat, the first nonsteroidal drug to treat patients with all genetic variants of Duchenne ...
MARCH 22, 2024
FDA Approves Agamree to Treat Duchenne Muscular Dystrophy
The FDA approved Agamree oral suspension for the treatment of Duchenne muscular dystrophy in children aged 24 ...
OCTOBER 27, 2023
More Data Needed Before Ataluren Can Be Recommended
In a 10-to-1 vote, the FDA’s Peripheral and Central Nervous System Drugs Advisory Committee said more data ...
SEPTEMBER 28, 2017
FDA Approves Drug to Treat Duchenne Muscular Dystrophy
The FDA today approved the orphan drug, Emflaza by Marathon Pharmaceuticals tablets and oral suspension to treat ...
FEBRUARY 9, 2017
FDA Approves Exondys 51 for Duchenne Muscular Dystrophy
This approval reflects the collective influence of the patient voice in drug approvals.
SEPTEMBER 21, 2016
